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Session Details

From FIH to Clinical Acceleration Plenary 'From Vision to Reality: Redefining the Frontier of Medicine
Friday, May 31, 2024 10:45 AM - 12:15 PM  
Plenary Hall
Plenary Session
Chair
  • Jacqueline Barry, PhD, Cell and Gene Therapy Catapult, United Kingdom
Speakers
  • Andrew Bellinger, MD, PhD, Verve Therapeutics, United States, "Single-Course GeneEditing Medicines and the Future Of Cardiovascular Care"
  • Julie Douville, PhD, n-Lorem Foundation, United States, "The n-Lorem Foundation: Redefining Medicine, One Patient at a Time"
  • William Hobbs, MD, PhD, Vertex Pharmaceuticals, United States, "Exa-cel: Development of the First Human Gene Editing Therapy"

Witness the application of CRISPR-edited cells to patients, revolutionizing the very fabric of genetic medicine. Delve into the promising realm of in vivo applications, envisioning a future where gene editing occurs directly within the human body. Explore the transformative potential of antisense technology in tackling ultra-rare genetic diseases, offering hope to individuals long overlooked by traditional medical approaches. Join us for an impactful journey into the exciting cell and gene therapy frontier where science fiction becomes medical reality. 

Jacqueline Barry
Chief Clinical Officer
Cell and Gene Therapy Catapult
Chair


Andrew Bellinger
Chief Scientific Officer
Verve Therapeutics
Speaker


Julie Douville
Executive Director of ASO Discovery and Development
n-Lorem Foundation
Speaker


William Hobbs
Vice President
Vertex Pharmaceuticals
Speaker