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Paula Rio PhD
Head of the Bone Marrow Aplasia Unit of the Hematopoietic Innovative Therapies Division
Centro de Investigaciones Energéticas, Medioambientales y Tecnológicas
Spain
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Paula Río is the head of the Bone Marrow Failure Unit at CIEMAT/CIBERER/IIS-FJD, UAM; Madrid. She has been working in the field of gene therapy of Fanconi anemia for more than 20 years, where she has focused on the design of a lentiviral vector for the correction of hematopoietic stem cells in patients with Fanconi anemia and its application in the clinic, with very promising results for patients. She is currently an associate researcher in two gene therapy clinical trials based on the preclinical studies developed by the group.
Since 2010 her work is focused on the search for new strategies to correct hematopoietic stem cells from FA patients by gene editing, a field in which she is coordinator of a European project and participates as principal investigator in other national and European projects.
She has published more than 55 papers in the field of gene therapy. She is a member of several scientific advisory committees, including the American Fanconi Anemia Research Foundation, the Gene Editing committees of the American Society for Gene Therapy and European Society for Gene and Cell Therapy and the Emerging Gene and Cell Therapies subcommittee from the American Society of Hematology.
Since 2010 her work is focused on the search for new strategies to correct hematopoietic stem cells from FA patients by gene editing, a field in which she is coordinator of a European project and participates as principal investigator in other national and European projects.
She has published more than 55 papers in the field of gene therapy. She is a member of several scientific advisory committees, including the American Fanconi Anemia Research Foundation, the Gene Editing committees of the American Society for Gene Therapy and European Society for Gene and Cell Therapy and the Emerging Gene and Cell Therapies subcommittee from the American Society of Hematology.